Koeks, Z; Bladen, CL; Salgado, D; van Zwet, E; Pogoryelova, O; McMacken, G; Monges, S; Foncuberta, M; Kekou, K; Kosma, K; Dawkins, H; Lamont, L; Bellgard, MI; Roy, AJ; Chamova, T; Guergueltcheva, V; Chan, S; Korngut, L; Campbell, C; Dai, Y; Wang, J; Barisic, N; Brabec, P; Lahdetie, J; Walter, MC; Schreiber-Katz, O; Karcagi, V; Garami, M; Herczegfalvi, Ágnes; Viswanathan, V; Bayat, F; Buccella, F; Ferlini, A; Kimura, E; van den Bergen, JC; Rodrigues, M; Roxburgh, R; Lusakowska, A; Kostera-Pruszczyk, A; Santos, R; Neagu, E; Artemieva, S; Rasic, VM; Vojinovic, D; Posada, M; Bloetzer, C; Klein, A; Diaz-Manera, J; Gallardo, E; Karaduman, AA; Oznur, T; Topaloglu, H; El, Sherif R; Stringer, A; Shatillo, AV; Martin, AS; Peay, HL; Kirschner, J; Flanigan, KM; Straub, V; Bushby, K; Beroud, C; Verschuuren, JJ; Lochmuller, H
(2017)
BACKGROUND: Recent short-term clinical trials in patients with Duchenne Muscular Dystrophy (DMD) have indicated greater disease variability in terms of progression than expected. In addition, as average life-expectancy ...